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TREATABLE DISEASES

APPROVED DISORDERS THAT COULD BE ADDRESSED USING STEM CELLS

  • Leukaemia’s: Leukaemia is a cancer of the blood immune system, cells are called leukocytes or white cells.

    • Acute Lymphoblastic Leukaemia (ALL)

    • Acute Myelogenous Leukaemia (AML)

    • Acute Biphenotypic Leukaemia

    • Acute Undifferentiated Leukaemia

    • Chronic Lymphocytic Leukaemia (CLL)

    • Chronic Myelogenous Leukaemia (CML)

    • Juvenile Chronic Myelogenous Leukaemia (JCML)

    • Juvenile Myelomonocytic Leukaemia (JMML)

 

  • Myelodysplastic Syndromes: Myelodysplastic Syndromes are also called pre-leukaemia.

    • Refractory Anaemia

    • Refractory Anaemia with Ringed Sideroblasts (Sideroblastic anemia)

    • Refractory Anaemia with Excess Blasts

    • Refractory Anaemia with Excess Blasts in Transformation

    • Chronic Myelomonocytic Leukaemia (CMML)

  • Lymphoma: Lymphoma is a cancer of the leukocytes that circulate in the blood and lymph vessels.

    • Hodgkin's Lymphoma

    • Non-Hodgkin's Lymphoma (Burkik's Lymphoma)

 

  • Transplants for Inherited Disorders: Transplants for Inherited Disorders of the Immune System and Other Organs.

    • Cartilage-Hair Hypoplasia

    • Erythropoitic Porphyria

    • Hermansky-Pudlak Syndrome

    • Pearson's Syndrome

    • Shwachman-Diamond Syndrome

    • Systemic Mastocytosis

 

  • Transplants for Inherited Metabolic Disorders: Mucopolysaccharidosis (MPS) Storage Diseases.

    • Hurler Syndrome (MPS-IH)

    • Scheie Syndrome (MPS-IS)

    • Hunter Syndrome (MPS-II)

    • Sanfilippo Syndrome (MPS-III)

    • Morquio Syndrome (MPS-IV)

    • Maroteaux-Lamy Syndrome (MPS-VI)

    • Sly Syndrome (MPS-VII) (beta-glucuronidase deficiency)

    • Mucolipidosis II (I-cell Disease)

 

  • Leukodystrophy Disorders

    • Adrenoleukodystrophy (ALD)

    • Krabbe Disease (Globoid Cell Leukodystrophy)

    • Metachromatic Leukodystrophy

    • Pelizaeus-Merzbacher Disease

 

  • Lysosomal Storage Diseases

    • Niemann-Pick Disease

    • Sandhoff Disease

    • Wolman Disease

 

  • Other Inherited Diseases

    • Lesch-Nyhan Syndrome

    • Osteopetrosis

 

  • Other Disorders of Blood Cell Proliferation: Anaemias are deficiencies or malformations of red cells.

    • Aplastic Anaemia

    • Fanconi Anaemia

    • Congenital Dyserythropoietic Anaemia

    • Paroxysmal Nocturnal Hemoglobinuria (PNH)

 

  • Inherited Red Cell Abnormalities: Red cells contain haemoglobin and carry oxygen to the body.

    • Sickle Cell Disease

    • Beta Thalassemia Major (aka Cooley's Anaemia)

    • Diamond-Blackfan Anaemia

    • Pure Red Cell Aplasia

 

  • Inherited Platelet Abnormalities: Platelets are blood cells needed for clotting.

    • Amegakaryocytosis / Congenital Thrombocytopenia

    • Glanzmann Thrombasthenia

 

  • Inherited Immune System Disorders: Severe Combined Immunodeficiency.

    • SCID with Adenosine Deaminase Deficiency (ADA-SCID)

    • SCID which is X-linked

    • SCID with absence of T & B Cells

    • SCID with absence of T Cells, Normal B Cells

    • Omenn Syndrome

 

  • Inherited Immune System Disorders: Neutropenia’s

    • Infantile Genetic Agranulocytosis (Kostmann Syndrome)

    • Myelokathexis

 

  • Inherited Immune System Disorders: Other

    • Ataxia-Telangiectasia

    • Bare Lymphocyte Syndrome

    • Common Variable Immunodeficiency

    • DiGeorge Syndrome

    • Haemophagocytic Lymphohistiocytosis

    • Leukocyte Adhesion Deficiency

    • Lymphoproliferative Disorders

    • Lymphoproliferative Disorder, X-linked (Susceptibility to Epstein-Barr virus)

    • Wiskok-Aldrich Syndrome

 

  • Myeloproliferative Disorders

    • Acute Myelofibrosis

    • Agnogenic Myeloid Metaplasia (Myelofibrosis)

    • Polycythemia Vera

    • Essential Thrombocythemia

 

  • Phagocyte Disorders: These are immune system cells that engulf and kill foreign organisms.

    • Chediak-Higashi Syndrome Chronic

    • Granulomatous Disease

    • Neutrophil Actin Deficiency

    • Reticular Dysgenesis

 

  • Bone Marrow Cancers

    • Multiple Myeloma

    • Plasma Cell Leukaemia

    • Waldenstrom's Macroglobulinemia Agnogenis Myeloid Metaplasia (Myelofibrosis)

 

  • Solid Tumours: Solid tumours not originating in the blood or immune system.

    • Neuroblastoma

    • Medulloblastoma

    • Retinoblastoma

HAVE QUESTIONS?

If you want to know more about these wonderful stem cells or require any other information on stem cells in general, please contact us and we will be happy to answer all your queries.

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